Novel Blood Biomarkers for Mucopolysaccharidosis Type III (Sanfilippo Disease)

Luzzi, A., Acevedo, J., Morales, A., Khijniak, M., Perez de la Garza, G., O’Neill, C., Chen, A., Iacovino, M., Eisengart, J., Polgreen, L.E., and Bitan, G.