Publications
A selected list of publications:
Vite Charles H, Nestrasil Igor, Mlikotic Anton, Jens Jackie K, Snella Elizabeth M, Gross William, Shapiro Elsa G, Kovac Victor, Provenzale James M, Chen Steven, Le Steven Q, Kan Shih-hsin, Banakar Shida, Wang Raymond Y, Haskins Mark E, Ellinwood N Matthew, Dickson Patricia I
Features of brain MRI in dogs with treated and untreated mucopolysaccharidosis type I Comparative medicine, 2013; 63(2): 163-73.
Vera Moin, Lester Thomas, Zhao Bin, Tiger Pascale, Clarke Scott, Tippin Brigette L, Passage Merry B, Le Steven Q, Femenia Javier, Lemontt Jeffrey F, Kakkis Emil D, Dickson Patricia I
Mannose 6-phosphate conjugation is not sufficient to allow induction of immune tolerance to phenylalanine ammonia-lyase in dogs JIMD reports, 2013; 8(2): 63-72.
Chen Agnes, Vogler Carole, McEntee Michael, Hanson Stephen, Ellinwood N Matthew, Jens Jackie, Snella Elizabeth, Passage Merry, Le Steven, Guerra Catalina, Dickson Patricia
Glycosaminoglycan storage in neuroanatomical regions of mucopolysaccharidosis I dogs following intrathecal recombinant human iduronidase APMIS : acta pathologica, microbiologica, et immunologica Scandinavica, 2011; 119(8): 513-21.
Dickson Patricia I, Hanson Stephen, McEntee Michael F, Vite Charles H, Vogler Carole A, Mlikotic Anton, Chen Agnes H, Ponder Katherine P, Haskins Mark E, Tippin Brigette L, Le Steven Q, Passage Merry B, Guerra Catalina, Dierenfeld Ashley, Jens Jackie, Snella Elizabeth, Kan Shih-Hsin, Ellinwood N Matthew
Early versus late treatment of spinal cord compression with long-term intrathecal enzyme replacement therapy in canine mucopolysaccharidosis type I Molecular genetics and metabolism, 2010; 101(2-3): 115-22.
Dierenfeld AD, McEntee MF, Passage M, Le S, Jens JK, Snella EM, Kline KL, Parkes JD, Ware WA, Moran LE, Wengert JA, Whitley RD, Betts DM, Boal AM, Riedesel EA, Gross W, Ellinwood NM, Dickson PI Replacing the enzyme α-L-iduronidase at birth ameliorates symptoms in the brain and periphery of dogs with mucopolysaccharidosis type I, Science Translational Medicine, 2010; 2(60): ra89.
Dickson Patricia, Peinovich Maryn, McEntee Michael, Lester Thomas, Le Steven, Krieger Aimee, Manuel Hayden, Jabagat Catherine, Passage Merry, Kakkis Emil D
Immune tolerance improves the efficacy of enzyme replacement therapy in canine mucopolysaccharidosis I The Journal of clinical investigation, 2008; 118(8): 2868-76.
Munoz-Rojas Maria-Veronica, Vieira Taiane, Costa Ronaldo, Fagondes Simone, John Angela, Jardim Laura Bannach, Vedolin Leonardo M, Raymundo Marcia, Dickson Patricia I, Kakkis Emil, Giugliani Roberto
Intrathecal enzyme replacement therapy in a patient with mucopolysaccharidosis type I and symptomatic spinal cord compression American journal of medical genetics. Part A, 2008; 146A(19): 2538-44.
Kakkis E, McEntee M, Vogler C, Le S, Levy B, Belichenko P, Mobley W, Dickson P, Hanson S, Passage M
Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I Molecular genetics and metabolism, 2004; 83(1-2): 163-74.
Dierenfeld Ashley D, McEntee Michael F, Vogler Carole A, Vite Charles H, Chen Agnes H, Passage Merry, Le Steven, Shah Sahil, Jens Jackie K, Snella Elizabeth M, Kline Karen L, Parkes Jennifer D, Ware Wendy A, Moran Lori E, Fales-Williams Amanda J, Wengert Jane A, Whitley R David, Betts Daniel M, Boal Amy M, Riedesel Elizabeth A, Gross William, Ellinwood N Matthew, Dickson Patricia I
Replacing the enzyme alpha-L-iduronidase at birth ameliorates symptoms in the brain and periphery of dogs with mucopolysaccharidosis type I Science translational medicine, 2010; 2(60): 60ra89.
Kishnani Priya S, Dickson Patricia I, Muldowney Laurie, Lee Jessica J, Rosenberg Amy, Abichandani Rekha, Bluestone Jeffrey A, Burton Barbara K, Dewey Maureen, Freitas Alexandra, Gavin Derek, Griebel Donna, Hogan Melissa, Holland Stephen, Tanpaiboon Pranoot, Turka Laurence A, Utz Jeanine J, Wang Yow-Ming, Whitley Chester B, Kazi Zoheb B, Pariser Anne R
Immune response to enzyme replacement therapies in lysosomal storage diseases and the role of immune tolerance induction Molecular genetics and metabolism, 2015; 28(6): .
Provenzale James M, Nestrasil Igor, Chen Steven, Kan Shih-Hsin, Le Steven Q, Jens Jacqueline K, Snella Elizabeth M, Vondrak Kristen N, Yee Jennifer K, Vite Charles H, Elashoff David, Duan Lewei, Wang Raymond Y, Ellinwood N Matthew, Guzman Miguel A, Shapiro Elsa G, Dickson Patricia I
Diffusion tensor imaging and myelin composition analysis reveal abnormal myelination in corpus callosum of canine mucopolysaccharidosis I Experimental neurology, 2015; 273(6): 1-10.
Dickson Patricia I, Kaitila Ilkka, Harmatz Paul, Mlikotic Anton, Chen Agnes H, Victoroff Alla, Passage Merry B, Madden Jacqueline, Le Steven Q, Naylor David E, Naylor David E
Safety of laronidase delivered into the spinal canal for treatment of cervical stenosis in mucopolysaccharidosis I Molecular genetics and metabolism, 2015; 116(1-2): 69-74.
Mendez Daniel C, Stover Alexander E, Rangel Anthony D, Brick David J, Nethercott Hubert E, Torres Marissa A, Khalid Omar, Wong Andrew Ms, Cooper Jonathan D, Jester James V, Monuki Edwin S, McGuire Cian, Le Steven Q, Kan Shih-Hsin, Dickson Patricia I, Schwartz Philip H
A novel, long-lived, and highly engraftable immunodeficient mouse model of mucopolysaccharidosis type I Molecular therapy. Methods & clinical development, 2015; 2(1-2): 14068.
Shah Anuja, Miller Clinton J, Nast Cynthia C, Adams Mark D, Truitt Barbara, Tayek John A, Tong Lili, Mehtani Parag, Monteon Francisco, Sedor John R, Clinkenbeard Erica L, White Kenneth, Mehrotra Rajnish, LaPage Janine, Dickson Patricia, Adler Sharon G, Iyengar Sudha K
Severe vascular calcification and tumoral calcinosis in a family with hyperphosphatemia: a fibroblast growth factor 23 mutation identified by exome sequencing Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association – European Renal Association, 2014; 29(12): 2235-43.
Kan Shih-Hsin, Aoyagi-Scharber Mika, Le Steven Q, Vincelette Jon, Ohmi Kazuhiro, Bullens Sherry, Wendt Daniel J, Christianson Terri M, Tiger Pascale M N, Brown Jillian R, Lawrence Roger, Yip Bryan K, Holtzinger John, Bagri Anil, Crippen-Harmon Danielle, Vondrak Kristen N, Chen Zhi, Hague Chuck M, Woloszynek Josh C, Cheung Diana S, Webster Katherine A, Adintori Evan G, Lo Melanie J, Wong Wesley, Fitzpatrick Paul A, LeBowitz Jonathan H, Crawford Brett E, Bunting Stuart, Dickson Patricia I, Neufeld Elizabeth F
Delivery of an enzyme-IGFII fusion protein to the mouse brain is therapeutic for mucopolysaccharidosis type IIIB Proceedings of the National Academy of Sciences of the United States of America, 2014; 111(41): 14870-5.
Wang Raymond Y, Aminian Afshin, McEntee Michael F, Kan Shih-Hsin, Simonaro Calogera M, Lamanna William C, Lawrence Roger, Ellinwood N Matthew, Guerra Catalina, Le Steven Q, Dickson Patricia I, Esko Jeffrey D
Intra-articular enzyme replacement therapy with rhIDUA is safe, well-tolerated, and reduces articular GAG storage in the canine model of mucopolysaccharidosis type I Molecular genetics and metabolism, 2014; 112(4): 286-93.
Vera Moin, Le Steven, Kan Shih-Hsin, Garban Hermes, Naylor David, Mlikotic Anton, Kaitila Ilkka, Harmatz Paul, Chen Agnes, Dickson Patricia
Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients Pediatric research, 2013; 74(6): 712-20.